Scientific Advisory Board

  • Brian Bettencourt, PhD

    Chair of Scientific Advisory Board

  • Dinah Sah, PhD

    Senior Advisor

  • Robert Desimone, PhD

    Director, McGovern Institute for Brain Research, MIT

  • John Rubenstein, MD, PhD

    Co-Founder, Neurona; Faculty Member at UC-San Francisco

  • Wendy Chung, MD, PhD

    Director of Clinical Genetics, Columbia University

  • Steven Wolf, MD

    Director of Pediatric Epilepsy, Boston Children’s Health Physicians

  • Eugene Schneider, MD

    VP and Head of Clinical Development, Ionis Pharmaceuticals

  • Petra Kaufmann, PhD

    VP, R&D, Translational Medicine at AveXis

  • Anna Greka, MD, PhD

    Institute Member, Broad Institute

  • Lauren Black, PhD

    Distinguished Scientist, Charles River Labs

  • Athma Pai, PhD

    Assistant Professor, RNA Therapeutics Institute, UMass Medical School

  • Matthew Lyst, PhD

    Molecular Biologist, University of Edinburgh

  • Patricia McGoldrick, NP, MPA, MSN

    Nurse Practitioner, Boston Children's Health Physicians

  • Summer Thyme, PhD

    Assistant Professor of Neurobiology at UAB

  • Lindsay Swanson, MS, CGC

    Genetic Counseling Program Manager, Boston Children’s Hospital

  • Ramon Y. Birnbaum, PhD

    Assistant Professor, Ben-Gurion University of the Negev

  • Bruria Ben-Zeev, MD

    Assistant Professor, Ben-Gurion University of the Negev

  • Dan DiPietro

    Partner, Aceras Life Sciences LLC; Co-founder, Modis Therapeutics

  • Steven Schreiber, MD

    Chief of Neurology, Tibor Rubin VA Medical Center

  • Lakshmi Mehta, MD, FACMG

    Director of Clinical Genetics, Icahn School of Medicine at Mount Sinai